Gene therapy is transplanting normal genes into cells in place of missing or defective ones, to correct the genetic disorders. (Google version >:D)
Loll, but that just means, replacing genes that are not working properly or missing with correct genes that work properly.
Gene therapy could be used to treat cystic fibrosis which is an inherited disease, meaning it is caused by defective genes and you are born with it. Meaning that you can't catch it, or develop it, you have it from when you are born. It also means that people born with it carrying the gene (Remember those who have cystic fibrosis have two homozygous recessive alleles For example 'rr', a carrier of cystic fibrosis may not necessarily have it themselves, but may have a heterozygous allele e.g. 'Rr' with only one small 'r' so if they 'canoodle' with someone who also has a heterozygous allele 'Rr' therefore also a carrier of cystic fibrosis and have a baby, that baby could be born with the disease as the may have inherited two homozygous recessive alleles 'rr'.) (I knowwwww, it's a mouthful, but focus!)
Now, Cystic fibrosis is caused by a defect in the CTFR gene which controls the production of a protein that controls the cell transport of chlorine ions in you bodaaaaayyyy. Sorry.
This disrupts the natural water potential ("The measure of the relative tendency…